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Treatment of spinal muscular atrophy cells with drugs that upregulate SMN expression reveals inter- and intra-patient variability
Also-Rallo, Eva, Alías, Laura, Martínez-Hernández, Rebeca, Caselles, Lidia, Barceló, María J, Baiget, Montserrat, Bernal, Sara, Tizzano, Eduardo FVolume:
19
Year:
2011
Language:
english
Pages:
7
DOI:
10.1038/ejhg.2011.89
File:
PDF, 549 KB
english, 2011