Self-complementary AAV-mediated gene therapy restores cone function and prevents cone degeneration in two models of Rpe65 deficiency
Pang, J, Boye, S E, Lei, B, Boye, S L, Everhart, D, Ryals, R, Umino, Y, Rohrer, B, Alexander, J, Li, JVolume:
17
Year:
2010
Language:
english
Pages:
12
DOI:
10.1038/gt.2010.29
File:
PDF, 1.13 MB
english, 2010