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In vivo post-transcriptional gene silencing of α-1 antitrypsin by adeno-associated virus vectors expressing siRNA
Cruz, Pedro E, Mueller, Christian, Cossette, Travis L, Golant, Alexandra, Tang, Qiushi, Beattie, Stuart G, Brantly, Mark, Campbell-Thompson, Martha, Blomenkamp, Keith S, Teckman, Jeffrey HVolume:
87
Year:
2007
Language:
english
Pages:
10
DOI:
10.1038/labinvest.3700629
File:
PDF, 393 KB
english, 2007