Transfusion independence and HMGA2 activation after gene therapy of human β-thalassaemia
Cavazzana-Calvo, Marina, Payen, Emmanuel, Negre, Olivier, Wang, Gary, Hehir, Kathleen, Fusil, Floriane, Down, Julian, Denaro, Maria, Brady, Troy, Westerman, KarenVolume:
467
Year:
2010
Language:
english
Pages:
5
DOI:
10.1038/nature09328
File:
PDF, 485 KB
english, 2010