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Allele-specific silencing of mutant huntingtin and ataxin-3 genes by targeting expanded CAG repeats in mRNAs
Hu, Jiaxin, Matsui, Masayuki, Gagnon, Keith T, Schwartz, Jacob C, Gabillet, Sylvie, Arar, Khalil, Wu, Jun, Bezprozvanny, Ilya, Corey, David RVolume:
27
Year:
2009
Language:
english
Pages:
7
DOI:
10.1038/nbt.1539
File:
PDF, 475 KB
english, 2009