Efficacy and long-term safety of alipogene tiparvovec (AAV1-LPLS447X) gene therapy for lipoprotein lipase deficiency: an open-label trial
Gaudet, D, Méthot, J, Déry, S, Brisson, D, Essiembre, C, Tremblay, G, Tremblay, K, de Wal, J, Twisk, J, van den Bulk, N, Sier-Ferreira, V, van Deventer, SLanguage:
english
Pages:
4
Journal:
Gene Therapy
DOI:
10.1038/gt.2012.43
Date:
June, 2012
File:
PDF, 613 KB
english, 2012