Use of Enzyme Replacement Therapy (Laronidase) before Hematopoietic Stem Cell Transplantation for Mucopolysaccharidosis I: Experience in 18 Patients
Robert F. Wynn, Jean Mercer, Joanne Page, Trevor F. Carr, Simon Jones, J. Edmond WraithVolume:
154
Year:
2009
Language:
english
Pages:
5
DOI:
10.1016/j.jpeds.2008.07.004
File:
PDF, 95 KB
english, 2009