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In vivo comparison of 2′-O-methyl phosphorothioate and morpholino antisense oligonucleotides for Duchenne muscular dystrophy exon skipping
Hans A. Heemskerk, Christa L. de Winter, Sjef J. de Kimpe, Petra van Kuik-Romeijn, Niki Heuvelmans, Gerard J. Platenburg, Gert-Jan B. van Ommen, Judith C. T. van Deutekom, Annemieke Aartsma-RusVolume:
11
Year:
2009
Language:
english
Pages:
10
DOI:
10.1002/jgm.1288
File:
PDF, 409 KB
english, 2009