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Direct central nervous system delivery provides enhanced protection following vector mediated gene replacement in a severe model of Spinal Muscular Atrophy
Jacqueline J. Glascock, Monir Shababi, Mary J. Wetz, Megan M. Krogman, Christian L. LorsonVolume:
417
Year:
2012
Language:
english
Pages:
382
DOI:
10.1016/j.bbrc.2011.11.121
File:
PDF, 952 KB
english, 2012