Enzyme replacement therapy (ENB-0040) in hypophosphatasia improves functional outcome and decreases TNSALP substrates in adolescents and adults
M.P. Whyte⁎, C.R. Greenberg, P. Kishnani, K. Madson, A. Mhanni, T.J. Weber, K. Mack, A. Reeves, H. Plotkin, N.C. Kreher, H. LandyVolume:
50
Year:
2012
Language:
english
Pages:
1
DOI:
10.1016/j.bone.2012.02.101
File:
PDF, 66 KB
english, 2012