G.P.3.05 Phase 2 study of PTC124 for nonsense mutation suppression therapy of Duchenne muscular dystrophy (DMD)
C. Bönnemann, R. Finkel, B. Wong, K. Flanigan, J. Sampson, L. Sweeney, A. Reha, G. Elfring, L. Miller, S. HirawatVolume:
17
Year:
2007
Language:
english
DOI:
10.1016/j.nmd.2007.06.080
File:
PDF, 46 KB
english, 2007