P2.09 A non-viral, GNE-lipoplex treatment to correct sialylation defects in hereditary inclusion body myopathy (HIBM)
T. Yardeni, I. Manoli, C. Ciccone, S. Hoogstraten-Miller, D. Darvish, Y. Anikster, P. Maples, C.M. Jay, W.A. Gahl, J. Nemunaitis, M. HuizingVolume:
20
Year:
2010
Language:
english
DOI:
10.1016/j.nmd.2010.07.081
File:
PDF, 48 KB
english, 2010