P4.40 Enzyme Replacement Therapy and prognostic factors for response: An ongoing open-label cohort study in adults with Pompe Disease
J.M. de Vries, N.A.M. van der Beek, M.L.C. Hagemans, W.C.J. Hop, A.J.J. Reuser, P.A. van Doorn, A.T. van der PloegVolume:
21
Year:
2011
Language:
english
DOI:
10.1016/j.nmd.2011.06.1005
File:
PDF, 49 KB
english, 2011