Beneficial effects of substrate reduction therapy in a mouse model of GM1 gangliosidosis
Elena Elliot-Smith, Anneliese O. Speak, Emyr Lloyd-Evans, David A. Smith, Aarnoud C. van der Spoel, Mylvaganam Jeyakumar, Terry D. Butters, Raymond A. Dwek, Alessandra d’Azzo, Frances M. PlattVolume:
94
Year:
2008
Language:
english
DOI:
10.1016/j.ymgme.2008.02.005
File:
PDF, 835 KB
english, 2008