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A dose-optimization trial of laronidase (Aldurazyme®) in patients with mucopolysaccharidosis I
Roberto Giugliani, Verónica Muñoz Rojas, Ana Maria Martins, Eugênia R. Valadares, Joe T.R. Clarke, José E.C. Góes, Emil D. Kakkis, Mary Alice Worden, Marisa Sidman, Gerald F. CoxVolume:
96
Year:
2009
Language:
english
DOI:
10.1016/j.ymgme.2008.10.009
File:
PDF, 258 KB
english, 2009