27. Substrate reduction therapy with miglustat in juvenile GM2 gangliosidosis
Joe T.R. Clarke, Gustavo H.B. Maegawa, Brenda Banwell, Susan Blaser, Paul van Giersbergen, Geoffrey Sorge, Maggie Tlopak, Cameron Arckerley, Cynthia Hawkins, Jason HayesVolume:
96
Year:
2009
Language:
english
DOI:
10.1016/j.ymgme.2008.11.028
File:
PDF, 43 KB
english, 2009