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Overexpression of adapted U1snRNA in patients' cells to correct a 5′ splice site mutation in propionic acidemia
Rocío Sánchez-Alcudia, Belén Pérez, Celia Pérez-Cerdá, M. Ugarte, Lourdes R. DesviatVolume:
102
Year:
2011
Language:
english
DOI:
10.1016/j.ymgme.2010.10.013
File:
PDF, 400 KB
english, 2011