Baseline data from a prospective international disease registry for Niemann-Pick disease type C
Marc Patterson, Eugen Mengel, Ed Wraith, Frits Wijburg, Marie Vanier, Barbara Schwierin, Audrey Muller, Mariabeth Silkey, Ruben Giorgino, Mercedes PinedaVolume:
102
Year:
2011
Language:
english
DOI:
10.1016/j.ymgme.2010.11.115
File:
PDF, 57 KB
english, 2011