Long Term Outcomes of a Phase 1/2, Multicenter, Open-Label, Dose-Escalation Study to Evaluate the Safety, Tolerability, and Efficacy of BMN 110 in Patients with Mucopolysaccharidosis IVA (Morquio A Syndrome)
Christian Hendriksz, Ashok Vellodi, Simon Jones, Hiwot Takkele, S. Lee, Sarah Chesler, Celeste DeckerVolume:
105
Year:
2012
Language:
english
DOI:
10.1016/j.ymgme.2011.11.076
File:
PDF, 57 KB
english, 2012