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Long circulating enzyme replacement therapy rescues bone pathology in mucopolysaccharidosis VII murine model
Daniel J. Rowan, Shunji Tomatsu, Jeffrey H. Grubb, Bisong Haupt, Adriana M. Montaño, Hirotaka Oikawa, Angela C. Sosa, Anping Chen, William S. SlyVolume:
107
Year:
2012
Language:
english
DOI:
10.1016/j.ymgme.2012.07.002
File:
PDF, 2.66 MB
english, 2012