Abstract: 554 AN OPEN-LABEL, DOSE ESCALATION STUDY TO ASSESS THE SAFETY AND EFFICACY OF AAV1-LPLS447X GENE THERAPY WITH ALIPOGENE TIPARVOVEC (AMT-011) FOR PATIENTS WITH SEVERE HYPERTRIGLYCERIDEMIA DUE TO LIPOPROTEIN LIPASE DEFICIENCY (LPLD)
Gaudet, D, Brisson, D, Methot, J, van Deventer, SVolume:
10
Language:
english
Journal:
Atherosclerosis Supplements
DOI:
10.1016/s1567-5688(09)70286-7
Date:
June, 2009
File:
PDF, 76 KB
english, 2009