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Enzyme Replacement Therapy in an Attenuated Case of Mucopolysaccharidosis Type I (Scheie Syndrome): A 6.5-Year Detailed Follow-Up
Agnieszka Jurecka, Jolanta Marucha, Elżbieta Jurkiewicz, Agnieszka Różdżyńska-Świątkowska, Anna Tylki-SzymańskaVolume:
47
Year:
2012
Language:
english
DOI:
10.1016/j.pediatrneurol.2012.08.010
File:
PDF, 444 KB
english, 2012