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A Randomized Study of Alglucosidase Alfa in Late-Onset Pompe's Disease
van der Ploeg, Ans T., Clemens, Paula R., Corzo, Deyanira, Escolar, Diana M., Florence, Julaine, Groeneveld, Geert Jan, Herson, Serge, Kishnani, Priya S., Laforet, Pascal, Lake, Stephen L., Lange, DalVolume:
362
Language:
english
Journal:
New England Journal of Medicine
DOI:
10.1056/NEJMoa0909859
Date:
April, 2010
File:
PDF, 350 KB
english, 2010