Enzyme replacement therapy with galsulfase in 34 children younger than five years of age with MPS VI
Horovitz, Dafne D.G., Magalhães, Tatiana S.P.C., Acosta, Angelina, Ribeiro, Erlane M., Giuliani, Liane R., Palhares, Durval B., Kim, Chong A., de Paula, Ana Carolina, Kerstenestzy, Marcelo, Pianovski,Volume:
109
Language:
english
Journal:
Molecular Genetics and Metabolism
DOI:
10.1016/j.ymgme.2013.02.014
Date:
May, 2013
File:
PDF, 636 KB
english, 2013