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Hereditary Inclusion Body Myopathy: Single Patient Response to Intravenous Dosing of GNE Gene Lipoplex
Nemunaitis, Gregory, Jay, Chris M., Maples, Phillip B., Gahl, William A., Huizing, Marjan, Yardeni, Tal, Tong, Alex W., Phadke, Anagha P., Pappen, Beena O., Bedell, Cynthia, Allen, Henry, Hernandez, CVolume:
22
Language:
english
Journal:
Human Gene Therapy
DOI:
10.1089/hum.2010.192
Date:
November, 2011
File:
PDF, 1.00 MB
english, 2011