The NCS-LSD cohort study: a description of the methods and analyses used to assess the long-term effectiveness of enzyme replacement therapy and substrate reduction therapy in patients with lysosomal storage disorders
Henley, W. E., Anderson, L. J., Wyatt, K. M., Nikolaou, V., Anderson, R., Logan, S.Volume:
37
Language:
english
Journal:
Journal of Inherited Metabolic Disease
DOI:
10.1007/s10545-014-9679-6
Date:
November, 2014
File:
PDF, 221 KB
english, 2014