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The clinical relevance of outcomes used in late-onset Pompe disease: can we do better?
Lachmann, Robin, Schoser, BenediktVolume:
8
Language:
english
Journal:
Orphanet Journal of Rare Diseases
DOI:
10.1186/1750-1172-8-160
Date:
December, 2013
File:
PDF, 377 KB
english, 2013