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Silencing Mutant ATXN3 Expression Resolves Molecular Phenotypes in SCA3 Transgenic Mice
Rodríguez-Lebrón, Edgardo, Costa, Maria doCarmo, Luna-Cancalon, Katiuska, Peron, Therese M, Fischer, Svetlana, Boudreau, Ryan L, Davidson, Beverly L, Paulson, Henry LVolume:
21
Language:
english
Journal:
Molecular Therapy
DOI:
10.1038/mt.2013.152
Date:
July, 2013
File:
PDF, 778 KB
english, 2013