![](/img/cover-not-exists.png)
Investigational intrathecal (IT) enzyme replacement therapy for the severe form of Hunter syndrome (mucopolysaccharidosis type II, MPS II)
Muenzer, Joseph, Hendriksz, Christian J., Stein, Margot B., Fan, Zheng, Kearney, Shauna, Horton, Johan, Vijayaraghavan, Suresh, Perry, Victor, Santra, Saikat, Solanki, Guirish A., Wang, Nan, Mascelli,Volume:
111
Language:
english
Journal:
Molecular Genetics and Metabolism
DOI:
10.1016/j.ymgme.2013.12.184
Date:
February, 2014
File:
PDF, 49 KB
english, 2014