Combination oral therapy for lysosomal gangliosidoses using FDA approved medications
Utz, Jeanine, Ziegler, Richard, Ahmed, Alia, Nestrasil, Igor, Karachunski, Peter, Bothun, Erick, Diethelm-Okita, Brenda, Whitley, Chester B.Volume:
108
Language:
english
Journal:
Molecular Genetics and Metabolism
DOI:
10.1016/j.ymgme.2012.11.257
Date:
February, 2013
File:
PDF, 56 KB
english, 2013