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P.4.10 Exon skipping as a therapeutic strategy applied to a RyR1 mutation causing severe core myopathy
Rendu, J., Brocard, J., Monnier, N., Piétri-Rouxel, F., Garcia, L., Lunardi, J., Fauré, J., Fourest-Lieuvin, A., Marty, I.Volume:
23
Language:
english
Journal:
Neuromuscular Disorders
DOI:
10.1016/j.nmd.2013.06.448
Date:
October, 2013
File:
PDF, 48 KB
english, 2013