Enzyme replacement therapy started at birth improves outcome in difficult-to-treat organs in mucopolysaccharidosis I mice
Baldo, Guilherme, Mayer, Fabiana Q., Martinelli, Bárbara Z., de Carvalho, Talita G., Meyer, Fabiola S., de Oliveira, Patrícia G., Meurer, Luise, Tavares, Ângela, Matte, Ursula, Giugliani, RobertoVolume:
109
Language:
english
Journal:
Molecular Genetics and Metabolism
DOI:
10.1016/j.ymgme.2013.03.005
Date:
May, 2013
File:
PDF, 1.57 MB
english, 2013