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Influence of Npc1 genotype on the toxicity of hydroxypropyl-β-cyclodextrin, a potentially therapeutic agent, in Niemann–Pick Type C disease models
Tanaka, Yuta, Ishitsuka, Yoichi, Yamada, Yusei, Kondo, Yuki, Takeo, Toru, Nakagata, Naomi, Higashi, Taishi, Motoyama, Keiichi, Arima, Hidetoshi, Matsuo, Muneaki, Higaki, Katsumi, Ohno, Kousaku, Irie,Volume:
1
Year:
2014
Language:
english
Journal:
Molecular Genetics and Metabolism Reports
DOI:
10.1016/j.ymgmr.2013.12.003
File:
PDF, 3.75 MB
english, 2014