Peptide Conjugation of 2′- O -methyl Phosphorothioate Antisense Oligonucleotides Enhances Cardiac Uptake and Exon Skipping in mdx Mice
Jirka, Silvana M.G., Heemskerk, Hans, Tanganyika-de Winter, Christa L., Muilwijk, Daan, Pang, Kar Him, de Visser, Peter C., Janson, Anneke, Karnaoukh, Tatyana G., Vermue, Rick, ‘t Hoen, Peter A.C., vaVolume:
24
Language:
english
Journal:
Nucleic Acid Therapeutics
DOI:
10.1089/nat.2013.0448
Date:
February, 2014
File:
PDF, 917 KB
english, 2014