![](/img/cover-not-exists.png)
Translation from a DMD exon 5 IRES results in a functional dystrophin isoform that attenuates dystrophinopathy in humans and mice
Wein, Nicolas, Vulin, Adeline, Falzarano, Maria S, Szigyarto, Christina Al-Khalili, Maiti, Baijayanta, Findlay, Andrew, Heller, Kristin N, Uhlén, Mathias, Bakthavachalu, Baskar, Messina, Sonia, Vita,Volume:
20
Language:
english
Journal:
Nature Medicine
DOI:
10.1038/nm.3628
Date:
August, 2014
File:
PDF, 1.47 MB
english, 2014