![](/img/cover-not-exists.png)
Pharmacological read-through of nonsense ARSB mutations as a potential therapeutic approach for mucopolysaccharidosis VI
Rosa Bartolomeo,Elena V. Polishchuk…Volume:
36
Language:
english
Journal:
Journal of Inherited Metabolic Disease
DOI:
10.1007/s10545-012-9521-y
Date:
March, 2013
File:
PDF, 488 KB
english, 2013