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Blood phenylalanine concentrations and dietary phenylalanine tolerance in patients with PKU in response to treatment with sapropterin hydrochloride: A multidimensional approach to determine clinically meaningful outcomes
Stockler-Ipsiroglu, Sylvia, Yuskiv, Nataliya, Apatean, Delia, Ueda, Keiko, Cheng, Barbara, Giezen, Alette, Salvarinova, Ramona, Lillquist, YolandaVolume:
47
Language:
english
Journal:
Clinical Biochemistry
DOI:
10.1016/j.clinbiochem.2014.07.041
Date:
October, 2014
File:
PDF, 44 KB
english, 2014