Evidence of Multiyear Factor IX Expression by AAV-Mediated Gene Transfer to Skeletal Muscle in an Individual with Severe Hemophilia B
JIANG, H, PIERCE, G, OZELO, M, DEPAULA, E, VARGAS, J, SMITH, P, SOMMER, J, LUK, A, MANNO, C, HIGH, KVolume:
14
Language:
english
Journal:
Molecular Therapy
DOI:
10.1016/j.ymthe.2006.05.004
Date:
September, 2006
File:
PDF, 242 KB
english, 2006