Reversal of Lysosomal Storage in Brain of Adult MPS-I Mice with Intravenous Trojan Horse-Iduronidase Fusion Protein
Boado, Ruben J., Hui, Eric Ka-Wai, Lu, Jeff Zhiqiang, Zhou, Qing-Hui, Pardridge, William M.Volume:
8
Language:
english
Journal:
Molecular Pharmaceutics
DOI:
10.1021/mp200136x
Date:
August, 2011
File:
PDF, 4.71 MB
english, 2011