Long-term developmental progression in infants and young children taking sapropterin for phenylketonuria: a two-year analysis of safety and efficacy
Longo, Nicola, Siriwardena, Komudi, Feigenbaum, Annette, Dimmock, David, Burton, Barbara K., Stockler, Sylvia, Waisbren, Susan, Lang, William, Jurecki, Elaina, Zhang, Charlie, Prasad, SuyashVolume:
17
Language:
english
Journal:
Genetics in Medicine
DOI:
10.1038/gim.2014.109
Date:
May, 2015
File:
PDF, 2.21 MB
english, 2015