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A Phase 1/2a Follistatin Gene Therapy Trial for Becker Muscular Dystrophy
Mendell, Jerry R, Sahenk, Zarife, Malik, Vinod, Gomez, Ana M, Flanigan, Kevin M, Lowes, Linda P, Alfano, Lindsay N, Berry, Katherine, Meadows, Eric, Lewis, Sarah, Braun, Lyndsey, Shontz, Kim, Rouhana,Volume:
23
Language:
english
Journal:
Molecular Therapy
DOI:
10.1038/mt.2014.200
Date:
January, 2015
File:
PDF, 3.22 MB
english, 2015