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Long-Term Preservation of Cones and Improvement in Visual Function Following Gene Therapy in a Mouse Model of Leber Congenital Amaurosis Caused by Guanylate Cyclase-1 Deficiency
Mihelec, Marija, Pearson, Rachael A., Robbie, Scott J., Buch, Prateek K., Azam, Selina A., Bainbridge, James W.B., Smith, Alexander J., Ali, Robin R.Volume:
22
Language:
english
Journal:
Human Gene Therapy
DOI:
10.1089/hum.2011.069
Date:
October, 2011
File:
PDF, 1.29 MB
english, 2011