Rapid deterioration of a patient with mucopolysaccharidosis type I during interruption of enzyme replacement therapy
Grzegorz Węgrzyn, Anna Tylki-Szymańska, Anna Liberek, Ewa Piotrowska, Joanna Jakóbkiewicz-Banecka, Jolanta Marucha, Barbara Czartoryska, Alicja WęgrzynVolume:
143A
Year:
2007
Language:
english
Pages:
3
DOI:
10.1002/ajmg.a.31831
File:
PDF, 82 KB
english, 2007