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Decreased corneal opacity and improved vision in a patient with mucopolysaccharidosis I (Hurler–Scheie) treated with enzyme replacement therapy (laronidase, Aldurazyme®)
Cristina Cáceres-Marzal, Mercedes García-Reymundo, Jorge Solana, Bernardo de Arévalo, Julián Vaquerizo, Enrique GalánVolume:
146A
Year:
2008
Language:
english
Pages:
3
DOI:
10.1002/ajmg.a.32317
File:
PDF, 194 KB
english, 2008