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Gene transfer of master autophagy regulator TFEB results in clearance of toxic protein and correction of hepatic disease in alpha-1-anti-trypsin deficiency
Pastore, Nunzia, Blomenkamp, Keith, Annunziata, Fabio, Piccolo, Pasquale, Mithbaokar, Pratibha, Maria Sepe, Rosa, Vetrini, Francesco, Palmer, Donna, Ng, Philip, Polishchuk, Elena, Iacobacci, Simona, PVolume:
5
Language:
english
Journal:
EMBO Molecular Medicine
DOI:
10.1002/emmm.201202046
Date:
March, 2013
File:
PDF, 1.87 MB
english, 2013