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In Vivo Evaluation of Candidate Allele-specific Mutant Huntingtin Gene Silencing Antisense Oligonucleotides
Southwell, Amber L, Skotte, Niels H, Kordasiewicz, Holly B, Østergaard, Michael E, Watt, Andrew T, Carroll, Jeffrey B, Doty, Crystal N, Villanueva, Erika B, Petoukhov, Eugenia, Vaid, Kuljeet, Xie, YuaVolume:
22
Language:
english
Journal:
Molecular Therapy
DOI:
10.1038/mt.2014.153
Date:
December, 2014
File:
PDF, 5.12 MB
english, 2014