Safety and Efficacy of Gene Transfer for Leber's Congenital Amaurosis
Maguire, Albert M., Simonelli, Francesca, Pierce, Eric A., Pugh, Edward N., Mingozzi, Federico, Bennicelli, Jeannette, Banfi, Sandro, Marshall, Kathleen A., Testa, Francesco, Surace, Enrico M., Rossi,Volume:
358
Language:
english
Journal:
New England Journal of Medicine
DOI:
10.1056/nejmoa0802315
Date:
May, 2008
File:
PDF, 515 KB
english, 2008