A Pilot Study of In Vivo Liver-Directed Gene Transfer with an Adenoviral Vector in Partial Ornithine Transcarbamylase Deficiency
Raper, Steven E., Yudkoff, Marc, Chirmule, Narendra, Gao, Guang-Ping, Nunes, Fred, Haskal, Ziv J., Furth, Emma E., Propert, Kathleen J., Robinson, Michael B., Magosin, Susan, Simoes, Heather, SpeicherVolume:
13
Language:
english
Journal:
Human Gene Therapy
DOI:
10.1089/10430340152712719
Date:
January, 2002
File:
PDF, 1.12 MB
english, 2002