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666. Conversion of βA- to βS-Globin by Small Fragment Homologous Replacement (SFHR) in Hematopoietic Stem/Progenitor Cells (HSPCs)
Abdolmohammadi, Alireza, Maurisse, Rosalie, Bedayat, Babak, De Semir, David, Wai-Men Cheung, Judy, Gruenert, Dieter C.Volume:
13
Language:
english
Journal:
Molecular Therapy
DOI:
10.1016/j.ymthe.2006.08.743
Date:
May, 2006
File:
PDF, 84 KB
english, 2006