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385. Tol2 Transposon as a Gene Therapy Vector: Characterization, Optimization and Correction of Hereditary Tyrosinemia Type 1 in Mouse
Balciunas, Darius, Wilber, Andrew, Wangensteen, Kirk, Bell, Jason, Geurts, Aron, Hackett, Perry B., Largaespada, David A., McIvor, R. Scott, Ekker, Stephen C.Volume:
13
Language:
english
Journal:
Molecular Therapy
DOI:
10.1016/j.ymthe.2006.08.446
Date:
May, 2006
File:
PDF, 82 KB
english, 2006